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Search Results for " PTC124 "
ターゲット
カタログ番号 |
製品名 |
別名 |
ターゲット |
T1805 |
Ataluren
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PTC124 |
CFTR
,
Autophagy
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Ataluren (PTC124) is a novel, orally administered drug that targets nonsense mutations. Ataluren is approved for use by the European Medicines Agency to treat Duchenne Muscular Dystrophy in patients aged 5 years and olde... |